Australia; International; NSW
An Australian and international trial has found that gene therapy for haemophilia can help reduce bleeding episodes as much as 4 years after the therapy, in contrast to earlier trials which suggested long term treatment could not be achieved this way. Previous gene therapy trials in patients with the bleeding disorder known as haemophilia A have shown promising initial results, but the therapy effect seemed to wear off after a few years. In this new study, 16 out of 18 patients showed improvement in blood clotting over a period of about 3 years and there was a 91.5 per cent reduction in the annual number of bleeding events.
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